Integration of Randomized Controlled Trials (RCTs) and Real-World Evidence (RWE) Data

Abstract Number:

1113 

Submission Type:

Invited Panel Session 

Participants:

Vipin Arora (1), Lehana Thabane (3), Jianchang Lin (4), Ilya Lipkovich (5), Theodore Lystig (5), Margaret Gamalo (2)

Institutions:

(1) Eli Lilly and Company, N/A, (2) Pfizer, N/A, (3) St. Joseph's Healthcare Hamilton, N/A, (4) Takeda, N/A, (5) N/A, N/A

Chair:

Margaret Gamalo  
Pfizer

Panelist(s):

Lehana Thabane  
St. Joseph's Healthcare Hamilton
Jianchang Lin  
Takeda
Ilya Lipkovich  
N/A
Theodore Lystig  
N/A

Session Organizer:

Vipin Arora  
Eli Lilly and Company

Session Description:

Intersectionality of RCTs and Registries and its Potential to Optimize Clinical Trial Operations can be challenging but remains critical. Registry data can be particularly valuable and well-utilized in certain therapeutic areas where they can provide comprehensive and real-world insights into disease progression, patient outcomes, treatment effectiveness, safety profiles. There are some therapeutic areas where registry data are more suitable and can be maximally utilized, e.g., oncology, rare diseases, transplantation, neurodegenerative and neuromuscular. In others, it is usually with regards to where they are used to gain insights of on effectiveness and safety of treatments irrespective of therapeutic area, e.g., pregnancy and reproductive health, pediatrics, and effects on cardiovascular outcomes. In these therapeutic areas, registry data can complement clinical trial data (RCTs) by providing insights from a broader and more diverse patient population, capturing real-world treatment patterns, and enabling long-term follow-up. Registry data are particularly valuable for observational studies, safety surveillance, health outcomes research, and comparative effectiveness studies. While the use registries numerous benefits, but it also comes with several challenges that need to be carefully addressed to ensure the quality, reliability, and ethical use of the data. These include selection bias and generalizability, data quality and completeness, confounding, endpoint definition and adjudication, longitudinal follow-Up and attrition, data privacy and security, data standardization and harmonization, data linkage and integration, ethical considerations, regulatory and compliance Issues. A panel from industry, academia and government will discuss their views on this topic at the invited panel.

Chair: Margaret Gamalo, PhD, FASA, VP- Pfizer Inc., PA, USA
Panelists:
Prof. Lehana Thabane, PhD, FASA, McMaster University, CANADA
Jianchang Lin, Ph.D., Senior Director, Statistics, Takeda Pharmaceutical Company Limited, Boston, MA, USA
Ilya Lipkovich, PhD, FASA, Executive Director, Eli Lilly and Company, Indianapolis, IN, USA
Theodore (Ted) Lystig, PhD, FASA, SVP, Chief Analytics Officer, Bridge Bio Therapeutics, CA, USA

Sponsors:

Biopharmaceutical Section 3
Caucus for Women in Statistics 2
Section for Statistical Programmers and Analysts 1

Theme: Statistics and Data Science: Informing Policy and Countering Misinformation

No

Applied

Yes

Estimated Audience Size

Medium (80-150)

I have read and understand that JSM participants must abide by the Participant Guidelines.

Yes

I understand and have communicated to my proposed speakers that JSM participants must register and pay the appropriate registration fee by June 1, 2024. The registration fee is nonrefundable.

I understand